Muscular dystrophy is a disease caused by mutations in the dystrophin gene. The muscles of muscular dystrophy patients weaken and atrophy over time. Heart and breathing muscles may also eventually be ...
Patients with the disease experience impaired mobility, heart and lung problems, and ultimately a shortened life expectancy. "Current gene therapy for Duchenne muscular dystrophy utilizes a truncated ...
Muscular dystrophy is a group of inherited conditions that lead to progressive weakening of voluntary muscles and, in some cases, impact the heart and other organs. There are nine major types of ...